Substance / Medication

Emicizumab

Overview

Active Ingredient
emicizumab
RxNorm CUI
1989794

Indications

HEMLIBRA is indicated for routine prophylaxis to prevent or reduce the frequency of bleeding episodes in adult and pediatric patients ages newborn and older with hemophilia A (congenital factor VIII deficiency) with or without factor VIII inhibitors.

Labeler: Genentech, Inc.Updated: 2025-07-11T00:00:00.000ZFull label on DailyMed

Boxed Warning

FDA Black Box Warning

Cases of thrombotic microangiopathy and thrombotic events were reported when on average a cumulative amount of >100 U/kg/24 hours of activated prothrombin complex concentrate was administered for 24 hours or more to patients receiving HEMLIBRA prophylaxis. Monitor for the development of thrombotic m

Contraindications

When this intervention should not be used

None.

Indications & Related Conditions

Conditions associated via SNOMED clinical relationships

Administration & Protocol

Dosing, route, and treatment protocol

Detailed dosage and administration information is available in the full FDA drug label.

View full prescribing information on DailyMed

Monitoring & Follow-Up

Biomarkers relevant to this intervention via related conditions

No monitoring biomarkers have been mapped yet. Biomarker-intervention linkages are derived through related conditions and will expand as the knowledge graph grows.

Clinical Trials

5 trials linked to this intervention

5
Total Trials
5
Recruiting
0
With Results

Research Evidence

Published studies and systematic reviews

Sort:
Efanesoctocog Alfa Versus Emicizumab in Adolescent and Adult Patients With Haemophilia A Without Inhibitors.
Álvarez Román María Teresa, Kragh Nana, Guyot Patricia et al. · Adv Ther · 2025
PMID: 39576432Meta-AnalysisFull text (PMC)
Cost-effectiveness of emicizumab for the treatment of hemophilia A: a systematic review.
Chen Min, Lin Yunzhu, He Guoqian et al. · Front Public Health · 2025
PMID: 41127589Meta-AnalysisFull text (PMC)
Emicizumab prophylaxis in people with hemophilia A and inhibitors: a systematic review and meta-analysis.
Prudente Tiago Paiva, Camelo Ricardo Mesquita, Guimarães Rafael Alves et al. · Sao Paulo Med J · 2024
PMID: 38747872Meta-AnalysisFull text (PMC)
Pharmacokinetics and Associated Efficacy of Emicizumab in Humans: A Systematic Review.
Donners Anouk A M T, Rademaker Carin M A, Bevers Lisanne A H et al. · Clin Pharmacokinet · 2021
PMID: 34389928Meta-AnalysisFull text (PMC)
Emicizumab for the treatment of haemophilia A: a narrative review.
Franchini Massimo, Marano Giuseppe, Pati Ilaria et al. · Blood Transfus · 2019
PMID: 31246563Meta-AnalysisFull text (PMC)
Emicizumab prophylaxis among infants and toddlers with severe hemophilia A and inhibitors-a single-center cohort.
Barg Assaf A, Avishai Einat, Budnik Ivan et al. · Pediatr Blood Cancer · 2019
PMID: 31348595RCT
Emicizumab in Previously Untreated Patients and Minimally Treated Patients With Hemophilia A: A Comparative Study Between Two International Cohorts.
Levy-Mendelovich Sarina, Barhod Tlalit, Budnik Ivan et al. · Pediatr Blood Cancer · 2026
PMID: 41126489Observational
Accurate evaluation of factor VIII activity of efanesoctocog alfa in the presence of emicizumab.
Nougier Christophe, Pipe Steven W, Pabinger Ingrid et al. · J Thromb Haemost · 2025
PMID: 39798924Observational

Research data from MEDLINE/PubMed

Benefits & Expected Outcomes

Benefits, expected outcomes, efficacy data, and NNT (Number Needed to Treat) are pending physician authorship and evidence review.

Risks & Side Effects

Adverse reaction and safety data for this drug is sourced from the FDA-approved label.

View adverse reactions & drug interactions on DailyMed

Related Symptoms

Symptoms associated with conditions this intervention addresses

No related symptoms have been mapped yet. Symptom linkages are derived through associated conditions.

Alternatives & Comparisons

Alternative treatments, comparison data, and clinical decision support are pending physician authorship.

Medical Disclaimer

This information is for educational purposes only and does not constitute medical advice, diagnosis, or treatment. Always consult with a qualified healthcare provider regarding any medical condition or treatment plan.

Do not start, stop, or change any treatment without consulting your healthcare provider.

Quick Facts

Type
Substance / Medication
Fully Specified Name
Emicizumab (substance)
SNOMED CT
763611007
UMLS CUI
C4278463
RxNorm CUI
1989794
Labeler
Genentech, Inc.

Clinical Data

This intervention maps to 1 entities in the Healos knowledge graph.

1
Conditions
0
Biomarkers
0
Specialists
0
Symptoms
5
Clinical Trials

Data is sourced from SNOMED CT, UMLS, and the Healos clinical knowledge graph. Content sections marked as pending require physician authorship. Consult a healthcare provider before starting any treatment.